Revision notes · Lecture 1 · Free

Introduction to health research

In one line: health research is any systematic study that produces knowledge to improve health. Before it starts, it faces three reviews: scientific, ethics and regulatory.

What this lecture's questions test

Out of the 30 questions on this lecture:

IdeaQuestions
The three reviews, and which approval is mandatory7
Types and scope of health research6
Planning a sound study6
Confounders and effect modifiers4
Pilot studies, and what is not a study design4
Random error and bias3

1. The three reviews

ReviewAsksLooks at
ScientificIs the science sound?Question, design, sample size, methods
EthicsAre participants protected?Consent, risks and benefits, privacy, the researcher's competence, care during and after
RegulatoryAre the laws followed?Funds and how they are used, samples or data sent abroad, intellectual property
  • Only ethics committee approval is mandatory for every study on people. The others depend on the study.
  • Peer review of a manuscript happens after the study, so it is not needed before starting one.
  • Setting up an institute's scientific committee is administration, not a step in your study.

Remember it: the science → scientific. The people → ethics. Money, borders, patents → regulatory.

2. Types of research

  • Bench (basic): in the laboratory, on animals or cells.
  • Clinical: on patients.
  • Translational: the bridge from bench to bedside.
  • Implementation: does a programme already known to work actually work on the ground? Acceptability, feasibility, delivery.
  • Health research covers disease burden, prevention and programme evaluation. It confirms what is known, finds what is new, and draws on biomedical science, biostatistics and social science.

3. Random error or bias?

Random errorSystematic error (bias)
CauseChanceA flaw in design, conduct or analysis
DirectionEither wayOne direction
Reduced byA bigger sample (never eliminated)Better design; sample size does not help

Trap: "better design eliminates random error" is false. Design fixes bias; sample size shrinks random error.

4. Confounder or effect modifier?

ConfounderEffect modifier
What it doesDistorts the association: linked to the exposure and, on its own, to the outcomeChanges the strength of a real association from one group to another
Deal with it byDesign (randomise, restrict, match) or analysis (stratify, adjust)Stratify and report each group separately; never adjust it away
ExampleSmoking, in a study of alcohol and lung cancerAge, when a vaccine protects children far better than older adults
  • Known effect modifiers come from a thorough literature review, not guesswork.

5. Pilot studies and study designs

  • A pilot study is a small rehearsal of the main study: it tests the tools, the sampling frame and feasibility, before main data collection. Ethics approval does not wait for it.
  • "Which is not a study design?" → pilot study or translational study. Those describe the size or purpose of a study, not its design.

6. Planning a sound study

  • The sample must be representative (external validity) and adequate (power). An adequate sample size is a prerequisite.
  • Inclusion and exclusion criteria must be specific and measurable.
  • Give every team member clear roles and responsibilities.
  • Plan on justification, a focused question and standard case definitions. Never financial gain.
  • Does a new vaccine programme reduce cases? → a field (randomised) trial.

Watch out: one question in this lecture combines a confounder statement with an effect-modifier statement that ends "…may be excluded from the study". The key and standard teaching disagree; the app explains it on that question.

Last look before the exam

  1. Only ethics approval is always mandatory.
  2. Intellectual property, samples or data abroad, funds → regulatory.
  3. Bigger sample → less random error. Better design → less bias.
  4. Confounder: adjust for it. Effect modifier: stratify and report.
  5. Pilot and translational studies are not study designs.

Practise lecture 1’s 30 questions